A drug in trials may help treat a slew of genetic disorders including Duchenne muscular dystrophy, cystic fibrosis, certain hemophilias. The drug,
PTC124, targets ribosomes, causing them to ignore nonsense mutations. Such mutations cause the translation of a protein to prematurely stop when a ribosome hits an erroneous stop codon. Will there be any side effect of ignoring all stop codons?
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